Search for Clinical Trials

Introduction: The melanocortin-4 receptor (MC4R) pathway is the principal regulator of mammalian energy balance and body weight. Originating in the…
  • Endocrinology
  • Genetic and Rare Diseases - Treatment
  • Pediatrics
RM-493-034: A 2-Stage (Open-Label Run-In Followed by Randomized Withdrawal), Double-Blind, Placebo-Controlled, Phase 2 Study of Setmelanotide In…
  • Genetic and Rare Diseases - Treatment
  • Endocrinology
  • Pediatrics
  • Obesity and Metabolism
Long Term Extension Trial Of Setmelanotide (RM-493) For Patients Who Have Completed A Trial Of Setmelanotide For The Treatment Of Obesity Associated…
  • Geriatrics
  • Genetic and Rare Diseases - Treatment
  • Endocrinology
  • Obesity and Metabolism
  • Nutrition
  • Digestive System
  • Diabetes
The goal of this study is to establish a database of pediatric patients with early-onset obesity who have been phenotypically well-characterized…
  • Growth and Development
  • Genetic and Rare Diseases - Treatment
  • Genetic and Rare Diseases - Observational and Gene Discovery
  • Endocrinology
  • Pediatrics
  • Obesity and Metabolism
  • Nutrition
  • Diabetes
To evaluate the rate of progression of choroideremia (as measured by several visual function tests and anatomical biomarkers). The intent is to offer…
  • Genetic and Rare Diseases - Treatment
  • Eye and Vision
A Multiple Site Phase  1/2, Safety and Efficacy Trial of AGTC-402, A Recombinant Adeno-Associated Virus Vector Expressing CNGA3, In Patients with…
  • Growth and Development
  • Genetic and Rare Diseases - Treatment
  • Eye and Vision
A Multiple Site Phase  1/2, Safety and Efficacy Trial of a Recombinant Adeno-Associated Virus Vector Expressing CNGB3 (RAAV2TYF-PR1.7-HCNGB3) In…
  • Genetic and Rare Diseases - Treatment
  • Eye and Vision
  • Pediatrics
Study Goal(s): To determine the effect of setmelanotide (RM-493) on weight, hunger assessments and other factors in patients with rare genetic…
  • Genetic and Rare Diseases - Treatment
  • Endocrinology
  • Pediatrics
  • Obesity and Metabolism
Study Goal(s): This Phase 3 study is designed to test the effectiveness and tolerability of intranasal carbetocin (LV-101),an oxytocin analog, in…
  • Genetic and Rare Diseases - Treatment
  • Endocrinology
  • Pediatrics
The purpose of this study is to select a suitable dose of BPS804 by measuring the strength/quality of bone using a special type of CT scanner.
  • Genetic and Rare Diseases - Treatment
Back to topback-to-top